Haemophilia trials in United States

In United States 42 Also abroad 128

42 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

Phase 4Not yet taking people in United States
Understanding Treatment Outcomes and Immunologic Mechanisms in Altuviiio Immune Tolerance Induction
Where
Milwaukee
Age
0 years to 17 years
People
15
Run by
Versiti Blood Health
See details and how to joinNCT07158606
No phaseNot yet taking people in United States
Study of a Smart Sharps Disposal Device in Patients With Hemophilia
Where
Philadelphia
Age
18 years and over
People
23
Run by
University of Pennsylvania
See details and how to joinNCT07421154
No phaseTaking people
Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis
Where
Boston, Chicago, Cincinnati, Detroit, Indianapolis, Little Rock, Oklahoma City, Palo Alto, San Diego, St. Petersburg
Age
6 years to 19 years
People
72
Run by
Wayne State University
See details and how to joinNCT05022459
Phase 1Taking people
A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)
Where
Ann Arbor, Chicago, Glendale, Greenville, Hershey, Los Angeles, Metairie, Philadelphia, St Louis
Age
18 years to 60 years
People
31 worldwide
Run by
Equilibra Bioscience LLC
See details and how to joinNCT06349473
No phaseTaking people
Efficacy, Safety & Utilisation of Nuwiq, Octanate and Wilate in Previously Untreated & Minimally Treated Haemophilia A Patients
Where
Las Vegas, Miami, New Orleans, San Antonio, St Louis
People
200 worldwide
Run by
Octapharma
See details and how to joinNCT03695978
Phase 4Taking people
Nuwiq for Perioperative Management Of Patients With Haemophilia A on Emicizumab Regular Prophylaxis Study
Where
Dallas
Age
12 years and over
People
28 worldwide
Run by
Octapharma
See details and how to joinNCT05935358
Phase 4Taking people
Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery
Where
San Antonio
Age
12 years and over
People
28 worldwide
Run by
Octapharma
See details and how to joinNCT05936580
No phaseTaking people
ATHNdataset Registry
Where
Hickory
People
200,000
Run by
American Thrombosis and Hemostasis Network
See details and how to joinNCT06820515
Phase 1Taking people
Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A
Where
Ann Arbor, Coral Gables, Hershey, Indianapolis, Kansas City, Madison, Mount Pleasant, Orange, Peoria, Redwood City, Seattle, Tampa
Age
0 years to 90 years
People
40
Run by
Bleeding and Clotting Disorders Institute Peoria, Illinois
See details and how to joinNCT05500807
No phaseTaking people
An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX® in Patients With Hemophilia B
Where
Rochester
Age
18 years and over
People
500 worldwide
Run by
CSL Behring
See details and how to joinNCT06008938
No phaseTaking people
Hemophilia A Research Program
Where
Seattle
People
500
Run by
University of Washington
See details and how to joinNCT07414511
No phaseEnrolling by invitation
Palliative Care Needs of Children With Rare Diseases and Their Families
Where
Washington D.C.
Age
12 months to 99 years
People
480
Run by
Children's National Research Institute
See details and how to joinNCT06938542
Phase 4Taking people
SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors
Where
Atlanta, Boston, Cleveland, Detroit, Greenville, Houston, Kansas City, Lansing, Little Rock, Los Angeles, Minneapolis, Nashville, New Hyde Park, Oklahoma City, Orlando, Phoenix, Rochester, Sacramento, Savannah, Washington D.C.
Age
12 years to 100 years
People
55
Run by
American Thrombosis and Hemostasis Network
See details and how to joinNCT04647227
Phase 4Enrolling by invitation
A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Where
Ann Arbor, Aurora, Columbus, Detroit, Los Angeles, Louisville, Pittsburgh, Sacramento, San Diego, San Francisco, Shandon, St Louis, Tampa
Age
18 years and over
People
172 worldwide
Run by
BioMarin Pharmaceutical
See details and how to joinNCT05768386 · EU 2023-507749-27-00
Phase 2/3Enrolling by invitation
Long-term Follow-up Study of Male Adults With Hemophilia B Previously Treated With Etranacogene Dezaparvovec (CSL222)
Where
Ann Arbor, Aurora, Chapel Hill, Houston, Little Rock, Los Angeles, Nashville, Phoenix, Portland, Sacramento, Salt Lake City, San Diego, Seattle, Tampa
Age
18 years and over
People
56 worldwide
Run by
CSL Behring
See details and how to joinNCT05962398 · EU 2023-503765-37-00
Phase 4Taking people
Hemlibra in Mild Hemophilia A
Where
Indianapolis
Age
5 years to 45 years
People
20
Run by
Indiana Hemophilia &Thrombosis Center, Inc.
See details and how to joinNCT04567511
Phase 1/2Taking people
ASC618 Gene Therapy in Hemophilia A Patients
Where
Little Rock
Age
18 years and over
People
12
Run by
ASC Therapeutics
See details and how to joinNCT04676048