Mitochondrial disease trials in Canada

4 trials · From ClinicalTrials.gov, checked 15 November 2026. Ask the study team whether a trial fits you.

• Phase 4Taking people
  Clinical Trial in Patients With Barth Syndrome- 4TAZPower

  Where

  Calgary

  Age

  5 years to 55 years

  People

  48 worldwide

  Run by

  Stealth BioTherapeutics Inc.

  See details and how to joinNCT07531251
• Phase 3Not yet taking people in Canada
  Efficacy and Safety of Modafinil to Treat Fatigue in People With Mitochondrial Disease.

  Where

  Montreal

  Age

  6 years to 60 years

  People

  15

  Run by

  Kenneth Myers, MD

  See details and how to joinNCT07887412
• Phase 2Taking people
  Deoxynucleosides Pyrimidines as Treatment for Mitochondrial Depletion Syndrome

  Where

  Montreal

  Age

  1 month to 60 years

  People

  200

  Run by

  Kenneth Myers, MD

  See details and how to joinNCT04802707
• No phaseTaking people
  North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  Where

  Hamilton

  People

  1,000 worldwide

  Run by

  Columbia University

  See details and how to joinNCT01694940