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Mitochondrial disease trials in United Kingdom
6 trials · From ClinicalTrials.gov, checked 15 November 2026. Ask the study team whether a trial fits you.
- Phase 4Taking peopleClinical Trial in Patients With Barth Syndrome- 4TAZPower
- Where
- Bristol
- Age
- 5 years to 55 years
- People
- 48 worldwide
- Run by
- Stealth BioTherapeutics Inc.
See details and how to joinNCT07531251 - Phase 3Taking peopleKHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases
- Where
- London
- Age
- 18 years to 64 years
- People
- 220 worldwide
- Run by
- Khondrion BV
See details and how to joinNCT06451757 · EU 2025-522361-30-00 - No phaseNot yet taking people in United KingdomProspective Natural History Study of POLG Disease
- Where
- Cambridge, London
- People
- 300 worldwide
- Run by
- The POLG Foundation
See details and how to joinNCT07775872 - Phase 2Taking peopleEfficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease
- Where
- Cambridge, London, Newcastle
- Age
- 18 years and over
- People
- 180 worldwide
- Run by
- Pharming Technologies B.V.
See details and how to joinNCT05650229 · EU 2023-508624-35-00 - No phaseTaking peopleMitochondrial Donation: An 18 Month Outcome Study.
- Where
- Newcastle upon Tyne
- People
- 25
- Run by
- Newcastle-upon-Tyne Hospitals NHS Trust
See details and how to joinNCT04113447 - No phaseTaking peopleNational Registry of Rare Kidney Diseases
- Where
- Bristol
- People
- 35,000
- Run by
- UK Kidney Association
See details and how to joinNCT06065852