Pompe disease trials in Australia

2 of 2 trials · From ClinicalTrials.gov, checked 12 November 2026. Ask the study team whether a trial fits you.

• No phaseTaking people
  Pompe Disease Registry Protocol

  Where

  Adelaide, Brisbane, Murdoch, Westmead

  People

  2,000 worldwide

  Run by

  Genzyme, a Sanofi Company

  See details and how to joinNCT00231400
• No phaseTaking people
  Pompe Pregnancy Sub-Registry

  Where

  Westmead

  People

  20 worldwide

  Run by

  Genzyme, a Sanofi Company

  See details and how to joinNCT00567073