Spinal muscular atrophy trials in Brazil

3 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

• No phaseTaking people
  A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma

  Where

  Curitiba, São Paulo

  Age

  0 years to 100 years

  People

  50

  Run by

  Novartis Pharmaceuticals

  See details and how to joinNCT06019637
• Phase 3Taking people
  A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  Where

  Distrito Federal, Porto Alegre, Sai Paula, São Paulo

  Age

  0 days to 42 days

  People

  30 worldwide

  Run by

  Biogen

  See details and how to joinNCT07221669 · EU 2025-524054-34-00
• Phase 1/2Taking people
  Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

  Where

  Porto Alegre

  Age

  2 weeks to 12 months

  People

  22

  Run by

  Gemma Biotherapeutics

  See details and how to joinNCT07070999