Spinal muscular atrophy trials in Canada

4 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

• Phase 2Taking people
  A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  Where

  Calgary, Toronto, Vancouver

  Age

  5 years to 17 years

  People

  60 worldwide

  Run by

  argenx

  See details and how to joinNCT07287982 · EU 2025-523496-32-00
• Phase 3Not yet taking people in Canada
  An Open Label Individual Patient (OLIP)-02 Study of Nusinersen (BIIB058)

  Where

  London

  People

  1

  Run by

  London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's

  See details and how to joinNCT07846696
• No phaseNot yet taking people in Canada
  An OLIP Study (Open Label Individual Patient) of Nusinersen in a Participant With Spinal Muscular Atrophy Who Previously Participated in an Investigational Study With Nusinersen

  Where

  London

  People

  1

  Run by

  London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's

  See details and how to joinNCT07838779
• No phaseTaking people
  A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophy

  Where

  Calgary, Halifax, Montreal, Toronto, Vancouver

  Age

  8 years to 18 years

  People

  22

  Run by

  Maryam Oskoui, MD, MSc, FRCPC, FAAN

  See details and how to joinNCT06396325