Spinal muscular atrophy trials in Italy

In Italy 9 Also abroad 68

9 trials · From ClinicalTrials.gov and EU CTIS (euclinicaltrials.eu), checked 11 November 2026. Ask the study team whether a trial fits you.

Phase 2Taking people
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Where
Milan, Rome
Age
Up to 17 years
People
30 worldwide
Run by
Scholar Rock Inc.
See details and how to join2024-520130-29-00 · EU 2024-520130-29-00
Phase 3Taking people
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Where
Milan
Age
0 days to 42 days
People
30 worldwide
Run by
Biogen
See details and how to joinNCT07221669 · EU 2025-524054-34-00
No phaseTaking people
Advanced Multi-omics and -System Approaches to Identify Novel Biomarkers for SMA
Where
Genova, Milan, Naples
People
200
Run by
Istituto Giannina Gaslini
See details and how to joinNCT07883655
Phase 3Taking people
A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Where
Milan, Rome
Age
0 days to 7 months
People
42 worldwide
Run by
Biogen
See details and how to joinNCT07444450 · EU 2025-523857-32-00
Phase 2Taking people
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Where
Milan, Rome
Age
Up to 2 years
People
52 worldwide
Run by
Scholar Rock, Inc.
See details and how to joinNCT07047144
Phase 1Taking people
A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Where
Milan, Rome
Age
3 years and over
People
78 worldwide
Run by
Biogen
See details and how to joinNCT06555419 · EU 2024-514239-21-00
No phaseTaking people
Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases
Where
Bosisio Parini, Conegliano
Age
18 years to 75 years
People
120
Run by
IRCCS Eugenio Medea
See details and how to joinNCT06666816
No phaseTaking people
Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments
Where
Genova, Messina, Milan, Rome
People
500
Run by
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
See details and how to joinNCT05768048
No phaseTaking people
Natural History of SMA
Where
Genova, Messina, Milan, Rome
People
1,200
Run by
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
See details and how to joinNCT05755451