Spinal muscular atrophy trials in Japan

3 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

• Phase 3Taking people
  A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  Where

  Tokyo

  Age

  0 days to 42 days

  People

  30 worldwide

  Run by

  Biogen

  See details and how to joinNCT07221669 · EU 2025-524054-34-00
• No phaseTaking people
  A Study of the Safety and Effectiveness of Onasemnogene Abeparvovec (Zolgensma) Intrathecal Injection in Spinal Muscular Atrophy Patients

  Where

  Fukuoka, Kodaira, Kyoto, Toyoake

  Age

  2 years and over

  People

  80

  Run by

  Novartis Pharmaceuticals

  See details and how to joinNCT07767890
• No phaseTaking people
  Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  Where

  Chiba, Fukui, Gifu, Hamamatsu, Hokkaido, Kita-gun, Kumamoto, Kurume-shi, Moriyama-shi, Nagakute-shi, Saitama, Sapporo, Sendai, Shimotsuke-shi, Shinjuku-ku, Shinjuku-Ku, Toyoake-shi, Yokohama

  People

  700 worldwide

  Run by

  Novartis Pharmaceuticals

  See details and how to joinNCT04174157