Thalassaemia: open trials in China

14 open trials have a site in China. Registry data; only the trial team decides who can take part.

NCT05991336
Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy
Research · Institute of Hematology & Blood Diseases Hospital, China
Regenerative Medicine Center, Tianjin
Registry updated 2026-11-04
NCT03351829
Gene Therapy of Beta Thalassemia Using a Self-inactivating Lentiviral Vector
Trial Treatment · Shenzhen Geno-Immune Medical Institute
Shenzhen Geno-immune Medical Institute, Shenzhen
Registry updated 2026-11-02
NCT06280378
β-Thalassemia Treatment With KL003 Cell Injection
Trial Treatment · Phase 1/2 · Kanglin Biotechnology (Hangzhou) Co., Ltd.
Ruijin Hospital Shanghai Jiaotong University School of Medicine, Shanghai · Institute of Hematology & Blood Diseases Hospital, Tianjin
Registry updated 2026-11-02
NCT06479616
A Long-term Follow-up Study in Participants Who Received CS-101
Trial Treatment · Children's Hospital of Fudan University
Children's Hospital Of Fudan University, Shanghai
Registry updated 2026-10-26
NCT04143724
Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia
Trial Treatment · Phase 2 · Celgene
West China Hospital，Sichuan University, Chengdu · Southern Medical University Nanfang Hospital, Guangzhou · Sun Yat-sen Memorial Hospital, Sun Yat-sen University, Guangzhou · People's Liberation Army The 923rd Hospital, Nanning · The First Affiliated Hospital of Guangxi Medical University, Nanning · Shenzhen Second People's Hospital, Shenzhen
Registry updated 2026-07-10
NCT04064060
A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials
Trial Treatment · Phase 3 · Celgene
Beijing · Chengdu · Guangzhou · Hangzhou · Shanghai · Tianjin
Registry updated 2026-07-01
NCT06328764
CS-101 in Patients With β-thalassemia
Trial Treatment · Early phase 1 · CorrectSequence Therapeutics Co., Ltd
The First Affiliated Hospital of Guangxi Medical University, Nanning
Registry updated 2026-06-09
NCT06685536
A Long-term Follow-up Study in Participants Who Received CS-101
Research · CorrectSequence Therapeutics Co., Ltd
The First Affiliated Hospital of Guangxi Medical University, Nanning
Registry updated 2026-02-10
NCT06717932
A Follow-up Study to Evaluate the Long-term Safety and Efficacy in Participants Who Received CS-101 Injection
Research · CorrectSequence Therapeutics Co., Ltd
The First Affiliated Hospital of Guangxi Medical University, Nanning
Registry updated 2026-02-10
NCT06772766
A Multiple Ascending Dose Study of 9MW3011 in Patients With Non-transfusion-dependent β-thalassemia
Trial Treatment · Phase 1 · Mabwell (Shanghai) Bioscience Co., Ltd.
Hainan General Hospital, Haikou · The First Affiliated Hospital of Guangxi Medical University, Nanning
Registry updated 2025-01-14
NCT06734520
Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemia
Trial Treatment · Guangzhou Women and Children's Medical Center
Guangzhou Women and Children's Medical Center Affiliated to Guangzhou Medical University, Guangzhou
Registry updated 2024-12-16
NCT06655662
Evaluating Safety and Efficacy of Lentiviral-transduced CD34+ HSCs in Β-thalassaemia Patients.
Trial Treatment · Phase 1 · Shenzhen Hemogen
Guangxi Medical University First Affiliated Hospital, Guangxi · Shenzhen university General Hospital, Shenzhen · Shenzhen Children's Hospital, Shenzhen
Registry updated 2024-10-23
NCT06465550
A Phase 1 Study of Gene-modified Autologous Hematopoietic Stem Cell (BD211) Treating β-thalassemia Major
Trial Treatment · Phase 1 · Shanghai BDgene Co., Ltd.
Sun Yat-sen Memorial Hospital, Guangzhou · The First Affiliated Hospital of Guangxi Medical University, Nanning · Shanghai Ruijin Hospital, Shanghai Jiaotong University, Shanghai
Registry updated 2024-06-24
NCT05762510
A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]
Trial Treatment · Early phase 1 · First Affiliated Hospital of Guangxi Medical University
The affiliated hospital of guangxi medical university, Nanning
Registry updated 2023-05-09

All Thalassaemia trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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