Thalassaemia trials in United States

28 trials · From ClinicalTrials.gov, checked 12 November 2026. Ask the study team whether a trial fits you.

• No phaseTaking people
  A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

  Where

  Houston, Minneapolis, New Hyde Park, Oakland, Palo Alto, Philadelphia

  People

  150

  Run by

  Genetix Biotherapeutics Inc.

  See details and how to joinNCT06271512
• No phaseEnrolling by invitation
  Decision-Making and Quality of Life Surrounding Hematologic Disease and Gene Therapy

  Where

  Washington D.C.

  Age

  18 years and over

  People

  100

  Run by

  Georgetown University

  See details and how to joinNCT06664541
• No phaseTaking people
  Study of the Role of Genetic Modifiers in Hemoglobinopathies

  Where

  Boston

  Age

  2 years and over

  People

  30,000 worldwide

  Run by

  Cyprus Institute of Neurology and Genetics

  See details and how to joinNCT05799118