Duchenne-izomdisztrófia: vizsgálatok itt: Franciaország

In Franciaország 17 Also abroad 87

17 trials · From ClinicalTrials.gov and EU CTIS (euclinicaltrials.eu), checked 2026. november 12.. Ask the study team whether a trial fits you.

3. fázisTaking people
A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Where
Nantes, Paris
Életkor
7 év to 16 év
People
70 worldwide
Run by
Avidity Biosciences, Inc.
See details and how to joinNCT07587242
3. fázisTaking people
Study in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
Where
Lille Cedex, Marseille, Nantes, Paris
Életkor
Up to 64 év
People
207 worldwide
Run by
Italfarmaco S.p.A.
See details and how to join2023-504520-26-00 · EU 2023-504520-26-00
No phaseNot yet taking people in Franciaország
Multimodal Study About Absence of Dp140 in Becker Muscular Dystrophy: Brain-muscle Imaging, Cognition and Muscle Function
Where
Paris
Életkor
18 év to 50 év
People
75
Run by
Institut de Myologie, France
See details and how to joinNCT07740057
No phaseTaking people
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
Where
Marseille
People
50
Run by
Assistance Publique Hopitaux De Marseille
See details and how to joinNCT06833489
No phaseTaking people
Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Where
Paris
Életkor
18 év and over
People
550
Run by
Assistance Publique - Hôpitaux de Paris
See details and how to joinNCT06147414
2/3. fázisTaking people
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy
Where
Bordeaux Cedex, Brest Cedex 2, Bron, Lille Cedex, Montpellier, Paris, Strasbourg Cedex 2
Életkor
6 év to 10 év
People
77 worldwide
Run by
Genethon
See details and how to joinNCT07856329 · EU 2023-505187-11-00
3. fázisTaking people
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Where
Paris, Strasbourg Cedex 2
Életkor
7 év to 11 év
People
80 worldwide
Run by
Solid Biosciences Inc.
See details and how to joinNCT07160634 · EU 2025-522949-22-00
2. fázisCsak meghívásos
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Where
Marseille, Nantes, Nice, Paris
People
260 worldwide
Run by
Edgewise Therapeutics, Inc.
See details and how to joinNCT06066580
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Where
Paris, Toulouse Cedex 9
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07037862 · EU 2024-517584-23-00
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Where
Bron, Paris, Toulouse Cedex 9
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07038824 · EU 2024-517499-39-00
3. fázisTaking people
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Where
Lille Cedex, Marseille, Paris
Életkor
9 év to 17 év
People
138 worldwide
Run by
Italfarmaco
See details and how to joinNCT05933057 · EU 2023-503521-19-00
No phaseTaking people
Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies
Where
Nantes
Életkor
5 év to 60 év
People
60
Run by
Nantes University Hospital
See details and how to joinNCT07378553
3. fázisTaking people
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
Where
Nantes, Paris
Életkor
Up to 17 év
People
42 worldwide
Run by
Avidity Biosciences Inc.
See details and how to join2025-523087-20-00 · EU 2025-523087-20-00
1/2. fázisTaking people
Phase 1/2a study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of SQY51 in Paediatric and Adult Patients with a Genetically Confirmed Diagnosis of Duchenne Muscular Dystrophy
Where
Garches
Életkor
Up to 64 év
People
12
Run by
Sqy Therapeutics
See details and how to join2022-500703-49-01 · EU 2022-500703-49-01
No phaseTaking people
Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies
Where
Clermont-Ferrand
Életkor
2 év and over
People
104
Run by
University Hospital, Clermont-Ferrand
See details and how to joinNCT07415837
No phaseTaking people
Natural History of Duchenne Muscular Dystrophy
Where
Bordeaux, Brest, Bron, Lille, Marseille, Montpellier, Paris, Strasbourg
Életkor
4 év to 9 év
People
220 worldwide
Run by
Genethon
See details and how to joinNCT03882827
2/3. fázisTaking people
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Where
Nantes, Paris
Életkor
7 év and over
People
206 worldwide
Run by
Italfarmaco
See details and how to joinNCT03373968