Pompe-betegség: vizsgálatok itt: Egyesült Királyság
5 trials · From ClinicalTrials.gov, checked 2026. november 12.. Ask the study team whether a trial fits you.
- No phaseTaking peoplePompe Disease Registry Protocol
- Where
- Birmingham, Cambridge, Cardiff, Glasgow, London, Manchester, Newcastle upon Tyne, Salford
- People
- 2000 worldwide
- Run by
- Genzyme, a Sanofi Company
See details and how to joinNCT00231400 - 2. fázisTaking peopleStudy of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Where
- Birmingham, London, Newcastle upon Tyne, Salford
- Életkor
- 18 év and over
- People
- 45 worldwide
- Run by
- Shionogi
See details and how to joinNCT07123155 - No phaseTaking peoplePompe Pregnancy Sub-Registry
- Where
- Cardiff
- People
- 20 worldwide
- Run by
- Genzyme, a Sanofi Company
See details and how to joinNCT00567073 - No phaseTaking peopleA Global Prospective Observational Registry of Patients With Pompe Disease
- Where
- Birmingham, Cambridge, Cardiff, London, Manchester, Salford
- People
- 500 worldwide
- Run by
- Amicus Therapeutics
See details and how to joinNCT06121011 - 3. fázisTaking peopleA Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
- Where
- London
- Életkor
- Up to 17 év
- People
- 36 worldwide
- Run by
- Amicus Therapeutics
See details and how to joinNCT04808505 · EU 2022-501095-25-01