Thalassaemia trials in Canada

In Canada 7 Also abroad 73

7 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

Phase 4Enrolling by invitation
A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study
Where
Hamilton, Toronto
Age
18 years and over
People
55 worldwide
Run by
Agios Pharmaceuticals, Inc.
See details and how to joinNCT05777993 · EU 2026-526243-35-00
Phase 3Taking people
A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia
Where
Montreal, Toronto, Vancouver
Age
2 years and over
People
480 worldwide
Run by
Novo Nordisk A/S
See details and how to joinNCT06609226 · EU 2024-510805-27-00
Phase 3Enrolling by invitation
A Long-term Follow-up Study in Participants Who Received CTX001
Where
Toronto, Vancouver
Age
2 years to 64 years
People
160 worldwide
Run by
Vertex Pharmaceuticals Incorporated
See details and how to joinNCT04208529 · EU 2024-512654-19-00
Phase 3Taking people
A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials
Where
Toronto
Age
18 years and over
People
665 worldwide
Run by
Celgene
See details and how to joinNCT04064060
Phase 1/2Enrolling by invitation
The BENeFiTS Trial in Beta Thalassemia Intermedia
Where
Toronto
Age
18 years and over
People
36 worldwide
Run by
Phoenicia BioScience
See details and how to joinNCT04432623
No phaseEnrolling by invitation
A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301
Where
Ottawa, Toronto
Age
12 years to 50 years
People
54 worldwide
Run by
Editas Medicine, Inc.
See details and how to joinNCT06363760
Phase 1/2Taking people
Thal-Fabs: Reduced Toxicity Conditioning for High Risk Thalassemia
Where
Toronto
Age
1 year to 18 years
People
20
Run by
The Hospital for Sick Children
See details and how to joinNCT05426252