Thalassaemia trials in United Kingdom

4 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

• Phase 4Enrolling by invitation
  A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study

  Where

  Manchester

  Age

  18 years and over

  People

  55 worldwide

  Run by

  Agios Pharmaceuticals, Inc.

  See details and how to joinNCT05777993 · EU 2026-526243-35-00
• Phase 3Taking people
  A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  Where

  London, Manchester, Sheffield

  Age

  2 years and over

  People

  480 worldwide

  Run by

  Novo Nordisk A/S

  See details and how to joinNCT06609226 · EU 2024-510805-27-00
• Phase 3Enrolling by invitation
  A Long-term Follow-up Study in Participants Who Received CTX001

  Where

  London

  Age

  2 years to 64 years

  People

  160 worldwide

  Run by

  Vertex Pharmaceuticals Incorporated

  See details and how to joinNCT04208529 · EU 2024-512654-19-00
• Phase 3Taking people
  A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials

  Where

  Aberdeen, Leeds, London, Oxford, Sutton in Ashfield

  Age

  18 years and over

  People

  665 worldwide

  Run by

  Celgene

  See details and how to joinNCT04064060