Duchenne-izomdisztrófia: vizsgálatok itt: Belgium

In Belgium 19 Also abroad 87

19 trials · From ClinicalTrials.gov and EU CTIS (euclinicaltrials.eu), checked 2026. november 12.. Ask the study team whether a trial fits you.

3. fázisTaking people
A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Where
Leuven, Liège
Életkor
7 év to 16 év
People
70 worldwide
Run by
Avidity Biosciences, Inc.
See details and how to joinNCT07587242
3. fázisTaking people
Study in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
Where
Leuven, Liège
Életkor
Up to 64 év
People
207 worldwide
Run by
Italfarmaco S.p.A.
See details and how to join2023-504520-26-00 · EU 2023-504520-26-00
2/3. fázisTaking people
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy
Where
Brussels, Leuven, Liège
Életkor
6 év to 10 év
People
77 worldwide
Run by
Genethon
See details and how to joinNCT07856329 · EU 2023-505187-11-00
2. fázisTaking people
A Phase 2 Open-label (Core Phase Plus Extension Phase) With 2 Cohorts Study to Assess the Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Than 6 Years Old
Where
Brussels
Életkor
Up to 17 év
People
10 worldwide
Run by
Italfarmaco S.p.A.
See details and how to join2024-511823-32-00 · EU 2024-511823-32-00
3. fázisTaking people
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Where
Brussels, Leuven
Életkor
7 év to 11 év
People
80 worldwide
Run by
Solid Biosciences Inc.
See details and how to joinNCT07160634 · EU 2025-522949-22-00
2. fázisCsak meghívásos
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Where
Ghent, Leuven, Liège
People
260 worldwide
Run by
Edgewise Therapeutics, Inc.
See details and how to joinNCT06066580
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Where
Gent, Leuven, Liège
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07037862 · EU 2024-517584-23-00
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Where
Gent, Leuven, Liège
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07038824 · EU 2024-517499-39-00
3. fázisTaking people
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Where
Leuven
Életkor
9 év to 17 év
People
138 worldwide
Run by
Italfarmaco
See details and how to joinNCT05933057 · EU 2023-503521-19-00
2. fázisNot yet taking people in Belgium
Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Evaluate the Safety and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE)
Where
Gent, Leuven, Liège
Életkor
4 év to 20 év
People
80 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07682129 · EU 2025-525124-10-00
No phaseNot yet taking people in Belgium
Digital Monitoring of Upper Limb Function in Non-Ambulant DMD
Where
Liège
People
50
Run by
Centre Hospitalier Universitaire de Liege
See details and how to joinNCT07664124
3. fázisTaking people
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
Where
Leuven, Liège
Életkor
Up to 17 év
People
42 worldwide
Run by
Avidity Biosciences Inc.
See details and how to join2025-523087-20-00 · EU 2025-523087-20-00
No phaseTaking people
Natural History of Duchenne Muscular Dystrophy
Where
Brussels, Leuven, Liège
Életkor
4 év to 9 év
People
220 worldwide
Run by
Genethon
See details and how to joinNCT03882827
3. fázisCsak meghívásos
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
Where
Gent
Életkor
Up to 64 év
People
400 worldwide
Run by
Sarepta Therapeutics, Inc.
See details and how to joinNCT05967351 · EU 2023-505043-39-00
2/3. fázisTaking people
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Where
Leuven, Liège
Életkor
7 év and over
People
206 worldwide
Run by
Italfarmaco
See details and how to joinNCT03373968
No phaseTaking people
Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening
Where
Liège
Életkor
4 hónap and over
People
100
Run by
Centre Hospitalier Universitaire de Liege
See details and how to joinNCT07286565
2. fázisTaking people
Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
Where
Brussels
Életkor
2 év to 6 év
People
18 worldwide
Run by
Italfarmaco
See details and how to joinNCT06769633
No phaseTaking people
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
Where
Liège
Életkor
1 év to 80 év
People
300 worldwide
Run by
Centre Hospitalier Universitaire de Liege
See details and how to joinNCT05982119
No phaseTaking people
Follow-up of NIV At Home in Patients with Duchenne Muscular Dystrophy
Where
Leuven
Életkor
18 év and over
People
17
Run by
Universitaire Ziekenhuizen KU Leuven
See details and how to joinNCT06773988