Myotonic dystrophy: vizsgálatok itt: Egyesült Államok

In Egyesült Államok 23 Also abroad 47

23 trials · From ClinicalTrials.gov, checked 2026. november 15.. Ask the study team whether a trial fits you.

3. fázisTaking people
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
Where
Atlanta, Baltimore, Columbia, Gainesville, Hillsborough, Houston, Indianapolis, La Jolla, Los Angeles, Palo Alto, Richmond, Rochester, Salt Lake City, San Antonio
Életkor
16 év to 64 év
People
150 worldwide
Run by
Dyne Therapeutics
See details and how to joinNCT07486934 · EU 2025-522957-20-00
No phaseTaking people
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Where
Columbus, Denver, Gainesville, Houston, Iowa City, Kansas City, La Jolla, Los Angeles, Richmond, Rochester
Életkor
18 év to 70 év
People
700 worldwide
Run by
Virginia Commonwealth University
See details and how to joinNCT03981575
No phaseTaking people
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Where
Fairway, Los Angeles, Richmond, Rochester
Életkor
Up to 59 hónap
People
50 worldwide
Run by
Virginia Commonwealth University
See details and how to joinNCT05224778
No phaseTaking people
Metabolomic Biomarkers of Myotonic Dystrophy
Where
Boston
Életkor
14 év and over
People
64
Run by
Massachusetts General Hospital
See details and how to joinNCT07912983
No phaseTaking people
Biomarker Development for Muscular Dystrophies
Where
Boston, Pittsburgh, Winston-Salem
Életkor
5 év and over
People
465
Run by
Massachusetts General Hospital
See details and how to joinNCT05019625
No phaseTaking people
Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy
Where
Boston
Életkor
18 év and over
People
88
Run by
Massachusetts General Hospital
See details and how to joinNCT06075693
No phaseTaking people
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
Where
Richmond
Életkor
18 év to 70 év
People
1000
Run by
Virginia Commonwealth University
See details and how to joinNCT07700225
2. fázisCsak meghívásos
A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type I
Where
Richmond, St Louis, Winston-Salem
Életkor
18 év to 64 év
People
44 worldwide
Run by
Vertex Pharmaceuticals Incorporated
See details and how to joinNCT06926621 · EU 2024-517983-47-00
No phaseTaking people
Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)
Where
Boston
Életkor
18 év to 70 év
People
24
Run by
Massachusetts General Hospital
See details and how to joinNCT06716931
1/2. fázisTaking people
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
Where
Gainesville, New York, Philadelphia, Richmond, Tampa
Életkor
10 év to 55 év
People
32 worldwide
Run by
Sanofi
See details and how to joinNCT06844214
3. fázisCsak meghívásos
Global Open-Label Extension Study of Del-desiran for the Treatment of DM1
Where
Baltimore, Boston, Cincinnati, Columbus, Denver, Durham, Gainesville, Houston, Indianapolis, Kansas City, Los Angeles, Minneapolis, Philadelphia, Richmond, Rochester, Seattle, Stanford, Tampa, Winston-Salem
Életkor
16 év to 64 év
People
199 worldwide
Run by
Avidity Biosciences, Inc.
See details and how to joinNCT07008469 · EU 2025-520766-22-00
No phaseTaking people
Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
Where
Kansas City, Little Rock, Richmond
Életkor
3 év to 17 év
People
200 worldwide
Run by
Virginia Commonwealth University
See details and how to joinNCT06747884
No phaseCsak meghívásos
Brain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2
Where
Winston-Salem
Életkor
30 év to 65 év
People
100
Run by
Wake Forest University Health Sciences
See details and how to joinNCT05854433
No phaseTaking people
Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
Where
Rochester
Életkor
0 év to 17 év
People
100
Run by
University of Rochester
See details and how to joinNCT07630389
3. fázisTaking people
Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
Where
Hillsborough
Életkor
4 év to 18 év
People
90
Run by
Dyne Therapeutics
See details and how to joinNCT07608432 · EU 2025-524096-23-00
No phaseTaking people
Remote Assessments and Genetic Determinants of Myotonic Dystrophy
Where
Rochester
Életkor
18 év to 88 év
People
1000
Run by
University of Rochester
See details and how to joinNCT07505342
1/2. fázisTaking people
Study of ATX-01 in Participants With DM1
Where
Fairway, Gainesville, Iowa City, Los Angeles, Richmond
Életkor
18 év to 64 év
People
56 worldwide
Run by
ARTHEx Biotech S.L.
See details and how to joinNCT06300307 · EU 2023-505363-37-00
No phaseTaking people
Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
Where
Winston-Salem
Életkor
18 év to 65 év
People
75
Run by
Wake Forest University Health Sciences
See details and how to joinNCT07362875
No phaseCsak meghívásos
Derivation of Human Induced Pluripotent Stem (iPS) Cells to Heritable Cardiac Arrhythmias
Where
Baltimore
Életkor
18 év to 85 év
People
100
Run by
Johns Hopkins University
See details and how to joinNCT02413450
No phaseTaking people
Long-Term Development of Muscular Dystrophy Outcome Assessments
Where
Richmond
Életkor
6 év to 50 év
People
1000
Run by
Virginia Commonwealth University
See details and how to joinNCT05989620
No phaseTaking people
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Where
Rochester
People
3000
Run by
University of Rochester
See details and how to joinNCT00082108
2/3. fázisTaking people
Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
Where
Chicago, Iowa City, Little Rock, Los Angeles, Norfolk, Palo Alto, Pittsburgh, Richmond, Rochester, Salt Lake City
Életkor
6 év to 45 év
People
76 worldwide
Run by
AMO Pharma Limited
See details and how to joinNCT05004129
No phaseTaking people
Myotonic Dystrophy Family Registry
Where
Oakland
People
3500
Run by
Myotonic Dystrophy Foundation
See details and how to joinNCT02398786