Duchenne-izomdisztrófia: vizsgálatok itt: Olaszország

In Olaszország 19 Also abroad 87

19 trials · From ClinicalTrials.gov and EU CTIS (euclinicaltrials.eu), checked 2026. november 12.. Ask the study team whether a trial fits you.

3. fázisTaking people
A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Where
Genova, Milan, Roma
Életkor
7 év to 16 év
People
70 worldwide
Run by
Avidity Biosciences, Inc.
See details and how to joinNCT07587242
3. fázisTaking people
Study in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
Where
Bosisio Parini, Genoa, Messina, Milan, Padova, Rome
Életkor
Up to 64 év
People
207 worldwide
Run by
Italfarmaco S.p.A.
See details and how to join2023-504520-26-00 · EU 2023-504520-26-00
No phaseTaking people
Bone Health in Adults With Duchenne Muscular Dystrophy: A Survey on Osteoporosis, Fractures and Treatment.
Where
Bologna, Bosisio Parini, Conegliano, Genova, Gussago, Messina, Milan, Naples, Padova, Pisa, Roma, Siena
Életkor
18 év to 44 év
People
200
Run by
Istituto Giannina Gaslini
See details and how to joinNCT07890883
No phaseTaking people
Respiratory Progression in Adults With Duchenne Muscular Dystrophy.
Where
Bologna, Bosisio Parini, Calambrone, Genova, Messina, Milan, Padova, Pavia, Pisa, Roma, Torino
Életkor
18 év and over
People
150
Run by
Istituto Giannina Gaslini
See details and how to joinNCT07879989
2. fázisTaking people
A Phase 2 Open-label (Core Phase Plus Extension Phase) With 2 Cohorts Study to Assess the Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Than 6 Years Old
Where
Milan, Rome
Életkor
Up to 17 év
People
10 worldwide
Run by
Italfarmaco S.p.A.
See details and how to join2024-511823-32-00 · EU 2024-511823-32-00
3. fázisTaking people
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Where
Milan, Rome
Életkor
7 év to 11 év
People
80 worldwide
Run by
Solid Biosciences Inc.
See details and how to joinNCT07160634 · EU 2025-522949-22-00
2. fázisCsak meghívásos
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Where
Milan, Padova, Rome
People
260 worldwide
Run by
Edgewise Therapeutics, Inc.
See details and how to joinNCT06066580
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Where
Milan, Rome
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07037862 · EU 2024-517584-23-00
1/2. fázisTaking people
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Where
Milan, Rome
Életkor
4 év to 20 év
People
24 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07038824 · EU 2024-517499-39-00
3. fázisTaking people
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Where
Milan, Padova, Ponte Lambro, Rome
Életkor
9 év to 17 év
People
138 worldwide
Run by
Italfarmaco
See details and how to joinNCT05933057 · EU 2023-503521-19-00
2. fázisCsak meghívásos
An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of BMN 351 in Participants With Duchenne Muscular Dystrophy
Where
Milan, Rome
Életkor
4 év to 64 év
People
18 worldwide
Run by
BioMarin Pharmaceutical
See details and how to joinNCT07573631 · EU 2024-511656-41-00
1/2. fázisTaking people
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Where
Rome
Életkor
0 év to 17 év
People
60 worldwide
Run by
Solid Biosciences Inc.
See details and how to joinNCT06138639 · EU 2024-514501-57-00
2. fázisNot yet taking people in Olaszország
Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Evaluate the Safety and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE)
Where
Milan, Rome
Életkor
4 év to 20 év
People
80 worldwide
Run by
Entrada Therapeutics, Inc.
See details and how to joinNCT07682129 · EU 2025-525124-10-00
3. fázisTaking people
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
Where
Genoa, Milan, Rome
Életkor
Up to 17 év
People
42 worldwide
Run by
Avidity Biosciences Inc.
See details and how to join2025-523087-20-00 · EU 2025-523087-20-00
3. fázisCsak meghívásos
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
Where
Genoa, Milan, Rome
Életkor
Up to 64 év
People
400 worldwide
Run by
Sarepta Therapeutics, Inc.
See details and how to joinNCT05967351 · EU 2023-505043-39-00
2/3. fázisTaking people
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Where
Genova, Messina, Milan, Roma
Életkor
7 év and over
People
206 worldwide
Run by
Italfarmaco
See details and how to joinNCT03373968
No phaseTaking people
Fear of Falling in Muscular Dystrophy
Where
Verona
Életkor
16 év to 65 év
People
100
Run by
Universita di Verona
See details and how to joinNCT07129954
No phaseNot yet taking people in Olaszország
Transition to Adulthood in People With Muscular Dystrophy
Where
Bosisio Parini
Életkor
14 év and over
People
250
Run by
IRCCS Eugenio Medea
See details and how to joinNCT07101185
2. fázisTaking people
Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
Where
Milan, Roma
Életkor
2 év to 6 év
People
18 worldwide
Run by
Italfarmaco
See details and how to joinNCT06769633