Gaucher-kór: nyitott vizsgálatok itt: Egyesült Államok

In Egyesült Államok 17 Also abroad 31

17 trials · From ClinicalTrials.gov, checked 2026. nov. 10.. Ask the study team whether a trial fits you.

No phaseToborozResearch participation
Natural History of Glycosphingolipid Storage Disorders and Glycoprotein Disorders
Where
Bethesda
Age
1 nap to 100 év
People
200
Run by
National Human Genome Research Institute (NHGRI)
See details and how to joinNCT00029965Regiszter frissítve: 2026-11-09
No phaseToborozResearch participation
Parkinson's Disease in Type 1 Gaucher Disease
Where
New York
Age
40 év and over
People
100
Run by
Icahn School of Medicine at Mount Sinai
See details and how to joinNCT07886879Regiszter frissítve: 2026-11-05
No phaseToborozResearch participation
Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease
Where
Minneapolis
Age
18 év to 75 év
People
34
Run by
University of Minnesota
See details and how to joinNCT02437396Regiszter frissítve: 2026-11-04
No phaseCsak meghívásosResearch participation
Genetic Studies of Lysosomal Storage Disorders
Where
Bethesda
Age
1 hét to 110 év
People
1000
Run by
National Human Genome Research Institute (NHGRI)
See details and how to joinNCT00001215Regiszter frissítve: 2026-10-29
No phaseToborozResearch participation
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
Where
Ann Arbor, Aurora, Baltimore, Beverly Hills, Boston, Camden, Charlotte, Charlottesville, Chicago, Cincinnati, Cleveland, Columbia, Columbus, Coral Gables, Coral Springs, Dallas, Decatur, Detroit, Dublin, Durham, Fairfax, Fort Worth, Grand Rapids, Greenville, Hackensack, Hershey, Huntington, Indianapolis, Iowa City, Jacksonville, Kansas City, Las Vegas, Little Rock, Los Angeles, Louisville, Milwaukee, Minneapolis, Morristown, Nashville, New Brunswick, New Haven, New Hyde Park, New Orleans, New York, Norfolk, Omaha, Orange, Paterson, Philadelphia, Phoenix, Pittsburgh, Portland, Providence, Rochester, Sacramento, Salt Lake City, San Diego, San Francisco, Seattle, Stanford, St Louis, Syracuse, Tacoma, Tampa, Tucson, Valhalla, Washington D.C.
People
12 000 worldwide
Run by
Genzyme, a Sanofi Company
See details and how to joinNCT00358943Regiszter frissítve: 2026-10-14
3. fázisToborozTrial-stage medicine
A Gaucher Disease Gene Therapy Trial With FLT201
Where
Atlanta, Aurora, Cincinnati, Dallas, Durham, Fairfax, Hackensack, Iowa City, Los Angeles, Minneapolis, New York, Philadelphia, Pittsburgh, San Francisco
Age
18 év and over
People
45 worldwide
Run by
Spur Therapeutics
See details and how to joinNCT07223944EU 2025-520765-50-00Regiszter frissítve: 2026-10-14
No phaseToborozResearch participation
Gaucher Disease Outcome Survey (GOS)
Where
Lexington
People
1257
Run by
Shire
See details and how to joinNCT03291223Regiszter frissítve: 2026-09-15
No phaseToborozResearch participation
A Long-term Follow-up Study of Gaucher Disease
Where
Durham
People
200
Run by
Duke University
See details and how to joinNCT03190837Regiszter frissítve: 2026-09-03
No phaseToborozResearch participation
Advancing Integrated Therapies for Gaucher Disease
Where
New Haven
Age
3 hónap to 75 év
People
30
Run by
Yale University
See details and how to joinNCT07758816Regiszter frissítve: 2026-08-11
No phaseToborozResearch participation
MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)
Where
Minneapolis
Age
18 év to 80 év
People
5
Run by
University of Minnesota
See details and how to joinNCT05586243Regiszter frissítve: 2026-08-04
No phaseCsak meghívásosResearch participation
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Where
Brooklyn, Manhasset, New York, Queens, The Bronx
Age
Up to 4 hét
People
100 000
Run by
Albert Einstein College of Medicine
See details and how to joinNCT05368038Regiszter frissítve: 2026-07-28
No phaseToborozResearch participation
Registry of Patients Diagnosed With Lysosomal Storage Diseases
Where
San Francisco
Age
Up to 64 év
People
250
Run by
University of California, San Francisco
See details and how to joinNCT05619900Regiszter frissítve: 2026-04-08
No phaseToborozResearch participation
Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease
Where
Minneapolis
Age
18 év to 80 év
People
30
Run by
University of Minnesota
See details and how to joinNCT05843552Regiszter frissítve: 2026-04-06
1. fázisToborozTrial-stage medicine
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Ez a vizsgálat csak várandós résztvevőket keres
Where
San Francisco
Age
18 év to 50 év
People
10
Run by
University of California, San Francisco
See details and how to joinNCT04532047Regiszter frissítve: 2026-03-17
No phaseToborozResearch participation
Longitudinal Study of Neurodegenerative Disorders
Where
Pittsburgh
People
1500
Run by
University of Pittsburgh
See details and how to joinNCT03333200Regiszter frissítve: 2026-02-09
No phaseToborozResearch participation
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Where
Pittsburgh
Age
2 hónap to 60 év
People
50
Run by
Paul Szabolcs
See details and how to joinNCT04528355Regiszter frissítve: 2026-01-13
2. fázisToborozTrial-stage medicine
Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Where
Pittsburgh
Age
2 hónap to 55 év
People
100
Run by
Paul Szabolcs
See details and how to joinNCT01962415Regiszter frissítve: 2025-12-15

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