Toboroz
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
NCT07506863· 3. fázis· Agios Pharmaceuticals, Inc.· Forrás
Toboroz
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia
NCT07517133· 3. fázis· Agios Pharmaceuticals, Inc.· Forrás
Toboroz
Study to evaluate the safety and efficacy of asciminib in pediatric participants with chronic myeloid leukemia.
2025-522138-29-00· 2. fázis· Novartis Pharma AG· Forrás
Toboroz
A Study to Learn More About How Safe Finerenone is, When it is Taken for a Longer Time With Standard Treatment, in Children and Young Adults With Heart Failure and Left Ventricular Systolic Dysfunction
NCT07192952· 3. fázis· Bayer· Forrás
Toboroz
A Study to Learn More About How Well Finerenone Works, How Safe it is, and How it Moves Into, Through, and Out of the Body Compared to Placebo When Taken With Standard Treatment in Children With Heart Failure and Left Ventricular Systolic Dysfunction
NCT07188805· 3. fázis· Bayer· Forrás
Toboroz
A Study of Patritumab Deruxtecan in Pediatric Participants With Relapsed or Refractory Solid Tumors (MK-9999-01C/LIGHTBEAM-U01)
NCT06941272· 1/2. fázis· Merck Sharp & Dohme LLC· Forrás
Fut, nem toboroz
Study to evaluate efficacy and safety of inclisiran in children aged 6 to under 12 years of age with heterozygous familial hypercholesterolemia.
2024-514594-21-00· 3. fázis· Novartis Pharma AG· Forrás
Fut, nem toboroz
Study to Provide Continued Access to Treatment for Patients Completing a Previous Trial With Efanesoctocog Alfa
NCT06716814· 3. fázis· Swedish Orphan Biovitrum· Forrás
Toboroz
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
NCT06612268· 3. fázis· Novo Nordisk A/S· Forrás
Toboroz
ALLIC 2022 international clinical investigation for advanced management of childhood acute lymphoblastic leukemia
2024-513824-41-00· 4. fázis· Semmelweis University· Forrás
Fut, nem toboroz
An open-label study to collect safety and effectiveness information on long-term treatment with vamorolone in boys with Duchenne Muscular Dystrophy
who have completed prior studies with vamorolone (The GUARDIAN Study)
2024-512828-12-00· 4. fázis· Santhera Pharmaceuticals (Schweiz) AG· Forrás
Fut, nem toboroz
LCH-IV International Collaborative Treatment Protocol for Children and Adolescents with Langerhans Cell Histiocytosis
NCT02205762· 2/3. fázis· St. Anna Childrens Cancer Research Institute GmbH· Forrás
Toboroz
Substudy 01A: Zilovertamab Vedotin in Pediatric and Young Adult Participants With Hematologic Malignancies or Solid Tumors (MK-9999-01A/LIGHTBEAM-U01)
NCT06395103· 1/2. fázis· Merck Sharp & Dohme LLC· Forrás
Fut, nem toboroz
Study to Assess Adverse Events, Change in Disease Activity, and How Oral Upadacitinib Moves Through the Body of Pediatric Participants With Moderately to Severely Active Ulcerative Colitis.
NCT05782907· 3. fázis· AbbVie· Forrás
Toboroz
A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes
NCT05693909· 2. fázis· Pharmacosmos A/S· Forrás
Toboroz
A Study of Vedolizumab in Children With Ulcerative Colitis (UC) or Crohn's Disease (CD)
NCT05442567· 3. fázis· Takeda· Forrás
Fut, nem toboroz
DAY101 vs. Standard of Care Chemotherapy in Pediatric Participants With Low-Grade Glioma Requiring First-Line Systemic Therapy (LOGGIC/FIREFLY-2)
NCT05566795· 3. fázis· Day One Biopharmaceuticals, Inc.· Forrás
Fut, nem toboroz
A Study to Test a Medicine (Fitusiran) Injected Under the Skin for Preventing Bleeding Episodes in Male Adolescent or Adult Participants With Severe Hemophilia
NCT05662319· 3. fázis· Sanofi· Forrás
Fut, nem toboroz
Phase 2 Study of Luspatercept in Adults and Adolescents with Alpha (α)-thalassemia
2022-502328-35-00· 2. fázis· Celgene Corp.· Forrás
Toboroz
Interfant-21 Treatment Protocol for Infants Under 1 Year With KMT2A-rearranged ALL or Mixed Phenotype Acute Leukemia
NCT05327894· 3. fázis· Princess Maxima Center for Pediatric Oncology· Forrás
Toboroz
A Study to Learn More About How Safe the Study Treatment Finerenone is in Long-term Use When Taken With an ACE Inhibitor or Angiotensin Receptor Blocker Over 18 Months of Use in Children and Young Adults From 1 to 18 Years of Age With Chronic Kidney Disease and Proteinuria
NCT05457283· 3. fázis· Bayer· Forrás
Toboroz
Biological Medicine for Diffuse Intrinsic Pontine Glioma (DIPG) Eradication 2.0
NCT05476939· 3. fázis· Gustave Roussy, Cancer Campus, Grand Paris· Forrás
Fut, nem toboroz
Study to determine the dose and safety of asciminib in pediatric patients with chronic myeloid leukemia.
2023-508129-28-00· 1/2. fázis· Novartis Pharma AG· Forrás
Toboroz
A Phase 2/3 Study of Osivelotor in Adult and Adolescent Participants With SCD
NCT05431088· 2/3. fázis· Pfizer· Forrás
Fut, nem toboroz
A Research Study to Compare Somapacitan Once a Week With Norditropin® Once a Day in Children Who Need Help to Grow
NCT05330325· 3. fázis· Novo Nordisk A/S· Forrás
Toboroz
International Euro Ewing (iEuroEwing) trial for treatment optimisation in patients with Ewing sarcoma
2022-501180-40-00· 3. fázis· GPOH gGmbH· Forrás
Fut, nem toboroz
A Study to Learn More About How Well the Study Treatment Finerenone Works, How Safe it is, How it Moves Into, Through, and Out of the Body, and the Effects it Has on the Body When Taken With an ACE Inhibitor or Angiotensin Receptor Blocker in Children With Chronic Kidney Disease and Proteinuria
NCT05196035· 3. fázis· Bayer· Forrás
Fut, nem toboroz
A Research Study on How Well Concizumab Works for You if You Have Haemophilia A or B With or Without Inhibitors
NCT05135559· 3. fázis· Novo Nordisk A/S· Forrás
Toboroz
Apremilast Pediatric Study in Children With Active Juvenile Psoriatic Arthritis
NCT04804553· 3. fázis· Amgen· Forrás
Toboroz
A Study of Vedolizumab in Children and Teenagers With Moderate to Severe Crohn's Disease (CD)
NCT04779320· 3. fázis· Takeda· Forrás
Fut, nem toboroz
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)
NCT04770753· 3. fázis· Agios Pharmaceuticals, Inc.· Forrás
Fut, nem toboroz
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
NCT04770779· 3. fázis· Agios Pharmaceuticals, Inc.· Forrás
Toboroz
FaR-RMS: An Overarching Study for Children and Adults With Frontline and Relapsed RhabdoMyoSarcoma
NCT04625907· 1/2. fázis· University of Birmingham· Forrás
Toboroz
SIOP RANDOMET 2017
2023-508926-91-00· 3. fázis· GPOH gGmbH· Forrás
Toboroz
High-Risk Neuroblastoma Study 2 of SIOP-Europa-Neuroblastoma (SIOPEN)
NCT04221035· 3. fázis· Gustave Roussy, Cancer Campus, Grand Paris· Forrás
Toboroz
SIOP Ependymoma II: An International Clinical Program for the diagnosis and treatment of children, adolescents and young adults with ependymoma
NCT02265770· 2/3. fázis· Centre Leon Berard· Forrás