Children's Memorial Health Institute

Futó vizsgálatok

• Toboroz

  A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

  NCT07444450· 3. fázis· Biogen· Forrás

• Még nem toboroz

  A Study to Evaluate Pharmacokinetics, Safety, Tolerability, Immunogenicity and Pharmacodynamic Effects of Subcutaneous Ocrelizumab Administration in Children and Adolescents With Relapsing-remitting Multiple Sclerosis (RRMS)

  NCT07503340· 2. fázis· Hoffmann-La Roche· Forrás

• Még nem toboroz

  Study of CDK8 Inhibitor RVU120 in Combination With Everolimus in Children With Recurrent or Progressive Group 3 or 4 Medulloblastoma

  NCT07865130· 1. fázis· Bożenna Dembowska Bagińska· Forrás

• Még nem toboroz

  Phase I study of CDK8 inhibitor RVU120 in combination with everolimus in children with recurrent or progressive Group 3 or 4 medulloblastoma; MEDWAY

  2025-524031-39-00· 1. fázis· Instytut Pomnik Centrum Zdrowia Dziecka· Forrás

• Toboroz

  Study to Assess Effects of Ublituximab in Pediatric Participants With Relapsing Forms of Multiple Sclerosis

  NCT07220252· 2/3. fázis· TG Therapeutics, Inc.· Forrás

• Toboroz

  A Study to Learn More About How Safe Finerenone is, When it is Taken for a Longer Time With Standard Treatment, in Children and Young Adults With Heart Failure and Left Ventricular Systolic Dysfunction

  NCT07192952· 3. fázis· Bayer· Forrás

• Toboroz

  A Study of How the Medicine Called "Etrasimod" Works in Children With the Gut Disease Called Ulcerative Colitis

  NCT07470879· 2. fázis· Pfizer· Forrás

• Toboroz

  A Study to Evaluate Pharmacokinetics, Efficacy, Safety, Tolerability, and Pharmacodynamics of Satralizumab in Pediatric Patients With Aquaporin-4 Antibody Positive Neuromyelitis Optica Spectrum Disorder (NMOSD)

  NCT05199688· 3. fázis· Hoffmann-La Roche· Forrás

• Fut, nem toboroz

  A Study to Find Out How EMPAgliflozin is Tolerated and if it Helps Children and Adolescents With Chronic KIDNEY Disease (EMPA-KIDNEY® Kids)

  NCT07107945· 3. fázis· Boehringer Ingelheim· Forrás

• Toboroz

  A Study to Learn More About How Well Finerenone Works, How Safe it is, and How it Moves Into, Through, and Out of the Body Compared to Placebo When Taken With Standard Treatment in Children With Heart Failure and Left Ventricular Systolic Dysfunction

  NCT07188805· 3. fázis· Bayer· Forrás

• Toboroz

  A Long-Term Extension Study of Vedolizumab in Children and Teenagers With Ulcerative Colitis (UC) or Crohn's Disease (CD)

  NCT06405087· 3. fázis· Takeda· Forrás

• Toboroz

  A Pharmacokinetics (PK), Pharmacodynamics (PD), Safety and Tolerability Study of Fenebrutinib in Children and Adolescents With Relapsing Multiple Sclerosis (RMS)

  NCT07161258· 2. fázis· Hoffmann-La Roche· Forrás

• Fut, nem toboroz

  A Protocol of Icotrokinra Therapy in Adult and Adolescent Participants With Moderately to Severely Active Ulcerative Colitis

  NCT07196748· 3. fázis· Janssen Research & Development, LLC· Forrás

• Toboroz

  A Study Evaluating the Effects of Filgotinib in Children and Teenagers With Ulcerative Colitis

  NCT06865417· 3. fázis· Alfasigma S.p.A.· Forrás

• Toboroz

  TAP-GRIN: Interventional Study on Patients With GRIN-related Neurodevelopmental Disorders

  NCT07377032· 3. fázis· Meyer Children's Hospital IRCCS· Forrás

• Toboroz

  A clinical trial in children and adolescents with primary malignant liver cancer - Hepatoblastoma and Hepatocarcinoma

  2024-514635-26-00· 3. fázis· Medical University Of Gdansk· Forrás

• Toboroz

  A study evaluating the effects of filgotinib in children and teenagers with ulcerative colitis

  2024-511458-32-00· 3. fázis· Alfasigma S.p.A.· Forrás

• Toboroz

  A Study of Vedolizumab in Children and Teenagers With Ulcerative Colitis or Crohn's Disease

  NCT06100289· 3. fázis· Takeda· Forrás

• Toboroz

  Study of the effectiveness of drugs selected depending on the molecular profile of diffuse intrinsic pontine glioma (DIPG).

  2024-515952-19-00· 2. fázis· Instytut Pomnik Centrum Zdrowia Dziecka· Forrás

• Toboroz

  A Long-term Extension (LTE) Study of Guselkumab in Pediatric Participants

  NCT06663332· 3. fázis· Janssen Research & Development, LLC· Forrás

• Toboroz

  This is a multicenter, double-blind, randomized study to compare the safety, effectiveness and immunogenicity (level and body resistance to drugs) of two biological drugs administered intravenously - vedolizumab (a drug not registered in pediatric patients) and infliximab (used as standard therapy) in pediatric patients with ulcerative colitis aged 6-17 years.

  2023-509775-16-00· 2. fázis· Instytut Pomnik Centrum Zdrowia Dziecka· Forrás

• Fut, nem toboroz

  STEP TEENS Weight Maintenance: A Research Study on How Well Semaglutide Helps Teenagers With Excess Body Weight to Lose Weight and Maintain Weight Loss

  NCT06571383· 4. fázis· Novo Nordisk A/S· Forrás

• Fut, nem toboroz

  A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  NCT05861999· 4. fázis· Hoffmann-La Roche· Forrás

• Fut, nem toboroz

  Crohn's Disease: Efficacy, Safety, and Pharmacokinetics of Upadacitinib in Pediatric Subjects With Moderately to Severely Active Crohn's Disease

  NCT06332534· 3. fázis· AbbVie· Forrás

• Fut, nem toboroz

  Astroscape: A Study of Radiprodil on Safety, Tolerability, Pharmacokinetics, and Effect on Seizures and Behavioral Symptoms in Patients With TSC or FCD Type II

  NCT06392009· 1/2. fázis· GRIN Therapeutics, Inc.· Forrás

• Fut, nem toboroz

  Development and Validation of a New Paediatric Inflammatory Bowel Disease NUTrition Risk Score (PIBD-NUTS)

  NCT06723418· University of Glasgow· Forrás

• Fut, nem toboroz

  A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  NCT05861986· 4. fázis· Hoffmann-La Roche· Forrás

• Toboroz

  A Study of Guselkumab in Pediatric Participants With Moderately to Severely Active Crohn's Disease

  NCT05923073· 3. fázis· Janssen Research & Development, LLC· Forrás

• Toboroz

  A Study of Mirikizumab (LY3074828) in Pediatric Participants With Crohn's Disease

  NCT05509777· 3. fázis· Eli Lilly and Company· Forrás

• Fut, nem toboroz

  A Study of Guselkumab in Pediatric Participants With Moderately to Severely Active Ulcerative Colitis

  NCT06260163· 3. fázis· Janssen Research & Development, LLC· Forrás

• Toboroz

  A Study to Assess Adverse Events, Change in Disease Activity, and How Intravenous and Subcutaneous Risankizumab Moves Through the Body of Pediatric Participants With Moderately to Severely Active Crohn's Disease

  NCT05995353· 3. fázis· AbbVie· Forrás

• Fut, nem toboroz

  Frexalimab in Preservation of Endogenous Insulin Secretion Compared to Placebo in Adults and Adolescents on Top of Insulin Therapy (FABULINUS)

  NCT06111586· 2. fázis· Sanofi· Forrás

• Fut, nem toboroz

  Study to Assess Adverse Events, Change in Disease Activity, and How Oral Upadacitinib Moves Through the Body of Pediatric Participants With Moderately to Severely Active Ulcerative Colitis.

  NCT05782907· 3. fázis· AbbVie· Forrás

• Toboroz

  A Study of Vedolizumab in Children With Ulcerative Colitis (UC) or Crohn's Disease (CD)

  NCT05442567· 3. fázis· Takeda· Forrás

• Fut, nem toboroz

  Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

  NCT05626855· 3. fázis· Scholar Rock, Inc.· Forrás

• Toboroz

  Placebo Controlled Study to Assess the Efficacy and Safety of Rapamycin in Drug Resistant Epilepsy Associated With Tuberous Sclerosis Complex

  NCT05534672· 3. fázis· Katarzyna Kotulska· Forrás

• Toboroz

  Study to Evaluate Sotatercept (MK-7962) in Children With Pulmonary Arterial Hypertension (PAH) (MK-7962-008)

  NCT05587712· 2. fázis· Merck Sharp & Dohme LLC· Forrás

• Toboroz

  A Study to Evaluate Etrasimod Treatment in Adolescents With Ulcerative Colitis

  NCT05287126· 2. fázis· Pfizer· Forrás

• Toboroz

  A Study to Learn More About How Safe the Study Treatment Finerenone is in Long-term Use When Taken With an ACE Inhibitor or Angiotensin Receptor Blocker Over 18 Months of Use in Children and Young Adults From 1 to 18 Years of Age With Chronic Kidney Disease and Proteinuria

  NCT05457283· 3. fázis· Bayer· Forrás

• Toboroz

  Open-label, Long-term Safety, Efficacy, and Pharmacokinetics Study of Vibegron in Pediatric Subjects 2 Years to < 18 Years of Age With NDO and on CIC

  NCT05491525· 2/3. fázis· Urovant Sciences GmbH· Forrás

• Fut, nem toboroz

  A Study to Learn About the Safety of BIIB115 Injections and How BIIB115 is Processed in the Bodies of Healthy Adult Male Volunteers and of Pediatric Participants With Spinal Muscular Atrophy Who Previously Took Onasemnogene Abeparvovec

  NCT05575011· 1. fázis· Biogen· Forrás

• Fut, nem toboroz

  A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy

  NCT05337553· 3. fázis· Biohaven Pharmaceuticals, Inc.· Forrás

• Toboroz

  International Wilson's Disease Patient Registry (iWilson Registry)

  NCT05239858· Orphalan· Forrás

• Fut, nem toboroz

  A Study to Evaluate Safety and Efficacy of Ocrelizumab in Comparison With Fingolimod in Children and Adolescents With Relapsing-remitting Multiple Sclerosis (RRMS)

  NCT05123703· 3. fázis· Hoffmann-La Roche· Forrás

• Toboroz

  A phase 2/3, multicenter, randomized, double-blind study to evaluate the efficacy, safety, pharmacokinetics and pharmacodynamics of oral ozanimod (RPC1063) in pediatric subjects with moderately to severely active ulcerative colitis with an inadequate response to conventional therapy.

  2023-509248-86-00· 2/3. fázis· Bristol-Myers Squibb Services Unlimited Company· Forrás

• Toboroz

  A Study of Vedolizumab in Children and Teenagers With Moderate to Severe Crohn's Disease (CD)

  NCT04779320· 3. fázis· Takeda· Forrás

• Toboroz

  Efficacy and safety of ofatumumab and siponimod compared to fingolimod in pediatric patients with multiple sclerosis

  2024-511686-11-00· 3. fázis· Novartis Pharma AG· Forrás

• Fut, nem toboroz

  Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative Colitis

  NCT04624230· 3. fázis· Pfizer· Forrás

• Toboroz

  Efficacy and Safety of Rapamycin Versus Vigabatrin in the Prevention of Tuberous Sclerosis Complex Symptoms in Infants

  NCT04987463· 2/3. fázis· Katarzyna Kotulska· Forrás

• Fut, nem toboroz

  Goat Infant Formula Feeding and Eczema (the GIraFFE Study)

  NCT04599946· Dairy Goat Co-operative (N.Z.) Limited· Forrás

Showing 50 of 58.

Egyszerre toboroz

Hány vizsgálat toboroz itt egyszerre ugyanarra az indikációra. Darabszám, nem értékelés.

• Colitis ulcerosa11 toboroz
• Gyermekkori daganatok9 toboroz
• Crohn-betegség8 toboroz
• Epilepszia3 toboroz
• Sclerosis multiplex (SM)3 toboroz
• Máj- és epeúti rák2 toboroz
• Szívelégtelenség2 toboroz
• Arthritis psoriatica1 toboroz
• Magas vérnyomás1 toboroz
• Neuromyelitis optica (NMOSD)1 toboroz
• Pikkelysömör1 toboroz
• Pulmonális artériás hipertónia1 toboroz
• Spinal cord injury1 toboroz
• Spinális izomatrófia (SMA)1 toboroz
• Wilson disease1 toboroz

Lezárt vizsgálatok

• Lezárult

  A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy

  NCT05808764· 2. fázis· Hoffmann-La Roche· Forrás

• Visszavonták

  A Study of Macitentan in Children Below 2 Years of Age

  NCT05731492· 1. fázis· Actelion· Forrás

• Lezárult

  A Study of Mirikizumab (LY3074828) in Pediatric Participants With Moderately to Severely or Active Ulcerative Colitis

  NCT05784246· 3. fázis· Eli Lilly and Company· Forrás

• Lezárult

  A Phase 3b Multicenter Open-label Trial of the Safety, Tolerability, and Efficacy of Tolvaptan in Infants and Children 28 days to less than 12 weeks of Age with Autosomal Recessive Polycystic Kidney Disease (ARPKD)

  NCT04786574· 3. fázis· Otsuka Pharmaceutical Development & Commercialization Inc.· Forrás

• Lezárult

  A Study to Investigate Behavioral and Other Co-Occurring Outcomes With Epidiolex as Add-On Therapy in Participants Aged 1 to 65 Years of Age With Tuberous Sclerosis Complex

  NCT05864846· 4. fázis· Jazz Pharmaceuticals· Forrás

• Lezárult

  Open-label study to assess safety and efficacy of rapamycin in drugresistant epilepsy associated with mTOR pathway pathologies

  2024-515950-25-00· 2. fázis· Instytut Pomnik Centrum Zdrowia Dziecka· Forrás

• Lezárult

  Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Oral Ozanimod in Pediatric Participants with Moderately to Severely Active Crohn's Disease with an Inadequate Response to Conventional Therapy

  2023-508777-91-00· 2/3. fázis· Celgene International II S.a.r.l.· Forrás

• Lezárult

  Clinical study to assess safety and efficacy of rapamycin in paediatric high grade glioma

  2024-515951-39-00· 2. fázis· Instytut Pomnik Centrum Zdrowia Dziecka· Forrás

• Toboroz

  A Study to See if Tolvaptan is Safe in Infants and Children Who at Enrollment Are 28 Days to Less Than 18 Years Old With Autosomal Recessive Polycystic Kidney Disease (ARPKD)

  NCT04782258· 3. fázis· Otsuka Pharmaceutical Development & Commercialization, Inc.· Forrás

• Lezárult

  Evaluation of the effect of phenofibrate on the functions of beta cells in children with new diagnosis of type 1 diabetes

  2024-517483-34-00· 2. fázis· Medical University Of Warsaw· Forrás

• Lezárult

  A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease

  NCT05218655· 3. fázis· PTC Therapeutics· Forrás

• Lezárult

  A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam (RO7034067) in Participants With Spinal Muscular Atrophy

  NCT05115110· 2/3. fázis· Hoffmann-La Roche· Forrás

• Lezárult

  Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

  NCT05156320· 3. fázis· Scholar Rock, Inc.· Forrás

• Fut, nem toboroz

  A Study to Learn More About How Well the Study Treatment Finerenone Works, How Safe it is, How it Moves Into, Through, and Out of the Body, and the Effects it Has on the Body When Taken With an ACE Inhibitor or Angiotensin Receptor Blocker in Children With Chronic Kidney Disease and Proteinuria

  NCT05196035· 3. fázis· Bayer· Forrás

• Lezárult

  A clinical study to investigate if the investigational drug Diamyd is safe and can preserve insulin production and secretion in adolescents and adults that have recently been diagnosed type 1 diabetes. The safety of Diamyd will also be investigated. Some subjects may receive a placebo drug.

  NCT05018585· 3. fázis· Diamyd Medical AB· Forrás

• Lezárult

  Basimglurant (NOE-101) in Children, Adolescents, and Young Adults With TSC

  NCT05059327· 2. fázis· Noema Pharma AG· Forrás

• Lezárult

  A Study of Vedolizumab in Children and Teenagers With Moderate to Severe Ulcerative Colitis (UC)

  NCT04779307· 3. fázis· Takeda· Forrás

• Lezárult

  A Study of Ustekinumab in Pediatric Participants With Moderately to Severely Active Crohn's Disease

  NCT04673357· 3. fázis· Janssen Research & Development, LLC· Forrás

• Lezárult

  A Study of Ustekinumab in Pediatric Participants With Moderately to Severely Active Ulcerative Colitis (UC)

  NCT04630028· 3. fázis· Janssen Research & Development, LLC· Forrás

• Lezárult

  A Phase 3 Study to Evaluate the Efficacy and Safety of Darvadstrocel in the Treatment of Complex Perianal Fistula in Pediatric Subjects with Crohn's Disease.

  NCT04701411· 3. fázis· Takeda Development Center Americas Inc.· Forrás

• Lezárult

  Prospective Study to Characterize the Pharmacokinetics and Pharmacodynamics of Cufence (Trientine Dihydrochloride) in Wilson Disease Patients

  2024-516431-27-00· 4. fázis· Univar Solutions B.V.· Forrás

• Leállították

  A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsy

  NCT04378075· 2/3. fázis· PTC Therapeutics· Forrás

• Lezárult

  Study of Nusinersen (BIIB058) in Participants With Spinal Muscular Atrophy

  NCT04089566· 3. fázis· Biogen· Forrás

• Lezárult

  A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease

  NCT03737214· 3. fázis· Idorsia Pharmaceuticals Ltd.· Forrás

• Lezárult

  Registry of Subjects With Drug Resistant Epilepsy and Treated With the VNS Therapy System.

  NCT03529045· LivaNova· Forrás

• Lezárult

  Study to Explore the Therapeutic Effect of Eluxadoline in Treating Irritable Bowel Syndrome With Diarrhea in Children

  NCT03339128· 2. fázis· AbbVie· Forrás

• Fut, nem toboroz

  Roll-over Study to Collect and Assess Long-term Safety of Everolimus in Patients With TSC and Refractory Seizures Who Have Completed the EXIST-3 Study [CRAD001M2304] and Who Are Benefitting From Continued Treatment

  NCT02962414· 3. fázis· Novartis Pharmaceuticals· Forrás

• Lezárult

  Phase 3 Efficacy and Safety Study of BG00012 in Pediatric Participants With Relapsing-Remitting Multiple Sclerosis (RRMS)

  NCT02283853· 3. fázis· Biogen· Forrás

Betegségek

Betegségek, amelyekről az intézmény publikál vagy amelyekre vizsgálatot futtat.

• Wilson disease3 munka · 2 vizsgálat